EFFICACY was studied in people aged 2 months to 25 years
SAFETY is being studied in people aged 2 months to 60 years
*FIREFISH is a 2-part, open-label study in 62 infants aged 2 to 7 months with Type 1 SMA. SUNFISH is a 2-part, placebo-controlled study in 231 adults and children aged 2 to 25 years with Type 2 or 3 SMA. JEWELFISH is an ongoing, open-label safety study in 174 people aged 1 to 60 years with Type 1, 2, or 3 SMA that was previously treated with approved or investigational SMA medications.
†In SUNFISH Part 1, 7 people were able to walk; in JEWELFISH, 16.
PART 1
PART 2
*Measured by the Motor Function Measure-32 Items (MFM-32) scale.
†Adults and children not taking Evrysdi took a placebo, a substance that has no active medication and is often used in studies.
PART 1
PART 2
*Measured by Item 22 of the Bayley Scales of Infant and Toddler Development–Third Edition (BSID-III) gross motor scale.
†Permanent support was defined as having a tracheostomy (a surgery where a tube is inserted in the front of the throat into the windpipe) or more than 21 days of either noninvasive ventilation support (16 or more hours a day) or being intubated (a procedure where a breathing tube is inserted down the throat and into the windpipe) to help with breathing, in the absence of an acute reversible event.
Sign up for additional information about Evrysdi and stay in the loop
Información de prescripción de Evrysdi® (risdiplam). Genentech, Inc.
Información de prescripción de Evrysdi® (risdiplam). Genentech, Inc.
The information contained in this section of the site is intended for U.S. healthcare professionals only. Click "OK" if you are a healthcare professional.
The link you have selected will take you away from this site to one that is not owned or controlled by Genentech, Inc. Genentech, Inc. makes no representation as to the accuracy of the information contained on sites we do not own or control. Genentech does not recommend and does not endorse the content on any third-party websites. Your use of third-party websites is at your own risk and subject to the terms and conditions of use for such sites.