Spinal muscular atrophy (SMA) is caused by a shortage of the survival motor neuron (SMN) protein, which your muscles need to function. As a result, muscles throughout your body continuously weaken.
This may lead to:
difficulty swallowing
difficulty eating
loss of motor function (for example, losing the ability to walk)
challenges breathing
Over time, it may cause complications with your bones, joints, and spine.
“There were no treatments for SMA until I was an adult. It wasn’t until I started to lose my hand strength that I decided to ask my doctor about treatment.”
“SMA can be subtle. Changes in strength can be gradual and hard to notice. You don’t know when, or what, or to what degree... but it’s relentless.”
Disease-modifying treatments have proven benefit across a broad range of ages and can help change the natural history of the disease.
“My biggest encouragement to others with SMA is to seek out treatment. Talk to your doctor. It can give you hope."
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Información de prescripción de Evrysdi® (risdiplam). Genentech, Inc.
Información de prescripción de Evrysdi® (risdiplam). Genentech, Inc.
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